Delivery Characterization of SPL84 Inhaled Antisense Oligonucleotide Drug for 3849 + 10 kb C- > T Cystic Fibrosis Patients

Efrat Ozeri-Galai, Lital Friedman, Ofra Barchad-Avitzur, Matthew R. Markovetz, William Boone, Kaitlyn R. Rouillard, Chava D. Stampfer, Yifat S. Oren, David B. Hill, Batsheva Kerem, Gili Hart

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